RNA splicing modulator-4
- Availability: 24/48H Stock Items & 2 to 6 Weeks non Stock Items.
- Dry Ice Shipment: No


RNA splicing modulator-4
Target:
DNA/RNA SynthesisRelated Pathways:
Cell Cycle/Checkpoint|||DNA Damage/DNA RepairBioactivity:
RNA splicing modulator-4 (Compound A) is an orally active, brain-penetrant, and selective modulator of RNA splicing. It regulates alternative splicing events to control the inclusion or exclusion of specific exons in precursor mRNA (pre-mRNA), thereby altering the coding sequence and function of mature mRNA. RNA splicing modulator-4 is promising for research in neurodegenerative diseases (such as Huntington's disease) and cancer.Smiles:
OC1=C(C=C2C(=C1)N=C(C)O2)C3=CC=C(N(C)[C@@H]4[C@H](F)[C@@]5(N[C@](C4)(CCC5)[H])[H])N=N3Molecular Formula:
C21H24FN5O2Molecular Weight:
397.45Shipping Conditions:
Cool packStorage Temperature:
-20°CCAS Number:
3067915-73-2
